From Clues to Care: Improving Recognition and Treatment of Alpha-Mannosidosis
* Integrated Care Coordination * Consensus Recommendations for Routine Follow-UpCare in AM * Detailed Assessment Recommendations by BodySystem
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4 episodios
Patient-Centered Holistic Care
Standard of Care Treatment and Monitoring for AM
* Enzyme Replacement Therapy (Velmanase Alfa) * Pivotal Trials of Velmanase Alfa in AM * Hematopoietic Stem Cell Transplant * Consensus Recommendations for Monitoring Treatment
Identification and Diagnosis of AM
* Phenotypic Subtypes of AMGuidelines for Genetic Testing * Diagnostic Algorithms for AM * Consensus Recommendations for Testing andBaseline Assessment
Introduction to Alpha-Mannosidosis (AM)
* Description * Epidemiology * Case Vignette
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¡Regístrate ahora y únete a la comunidad de From Clues to Care: Improving Recognition and Treatment of Alpha-Mannosidosis!